A Cultured Leukemia Stem Cell Model Enables Validation of CDK6 as a Stemness Target Against Acute Myeloid Leukemia
Acute myeloid leukemia (AML) represents a group of aggressive hematological malignancies, the clinical management of which is made challenging due to the persistence of rare and therapy resistant leukemia stem cells (LSCs) which serve as a source of disease relapse and poor outcomes. There are currently a paucity of methods to reliably enrich and study LSCs, hindering the development of therapies that specifically target LSCs. In this study, we deeply characterize the OCI-AML8227 culture model, which maintains a functional stemness hierarchy originating from its highly primitive CD34⁺CD38⁻ cells, to elucidate LSC biology and uncover LSC-specific therapeutic vulnerabilities. We analyzed both bulk and single-cell proteomics, transcriptomics, and epigenomics to generate a LSC protein-protein interaction network, which was then integrated with an LSC-focused small molecule screen using this model. From these findings, CDK6 was discovered as a therapeutic vulnerability specific to LSCs, which was validated in findings from the BEAT-AML cohort and a patient-derived xenograft (PDX) panel of AML samples through palbociclib treatment. Taken together, our studies validate CDK6 as a druggable vulnerability in LSCs, and authenticate OCI-AML8227 cells as a LSC target discovery engine.
- 27/03/2025
- 30 samples
- DAC: EGAC00000000011
- Technologies: Illumina HiSeq 2500, Illumina NovaSeq 6000
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Studies are experimental investigations of a particular phenomenon, e.g., case-control studies on a particular trait or cancer research projects reporting matching cancer normal genomes from patients.
Study ID | Study Title | Study Type |
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EGAS50000000786 | RNASeq | |
EGAS50000000787 | Epigenetics | |
EGAS50000000788 | Epigenetics | |
EGAS50000000789 | RNASeq |
This table displays only public information pertaining to the files in the dataset. If you wish to access this dataset, please submit a request. If you already have access to these data files, please consult the download documentation.
ID | File Type | Size | Located in | |
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EGAF50000277486 | fastq.gz | 3.7 GB | ||
EGAF50000277487 | fastq.gz | 3.7 GB | ||
EGAF50000277488 | fastq.gz | 3.8 GB | ||
EGAF50000277489 | fastq.gz | 3.4 GB | ||
EGAF50000277490 | fastq.gz | 3.0 GB | ||
EGAF50000277491 | fastq.gz | 2.5 GB | ||
EGAF50000277492 | fastq.gz | 3.8 GB | ||
EGAF50000277493 | fastq.gz | 3.9 GB | ||
EGAF50000277494 | fastq.gz | 3.3 GB | ||
EGAF50000277495 | fastq.gz | 3.4 GB | ||
EGAF50000277496 | fastq.gz | 3.1 GB | ||
EGAF50000277497 | fastq.gz | 3.2 GB | ||
EGAF50000277498 | fastq.gz | 3.6 GB | ||
EGAF50000277499 | fastq.gz | 3.5 GB | ||
EGAF50000277500 | fastq.gz | 2.6 GB | ||
EGAF50000277501 | fastq.gz | 2.6 GB | ||
EGAF50000277502 | fastq.gz | 2.7 GB | ||
EGAF50000277503 | fastq.gz | 3.4 GB | ||
EGAF50000277504 | fastq.gz | 3.6 GB | ||
EGAF50000277505 | fastq.gz | 3.8 GB | ||
EGAF50000277506 | fastq.gz | 3.7 GB | ||
EGAF50000277507 | fastq.gz | 3.7 GB | ||
EGAF50000277508 | fastq.gz | 3.5 GB | ||
EGAF50000277509 | fastq.gz | 3.6 GB | ||
EGAF50000277510 | fastq.gz | 2.9 GB | ||
EGAF50000277511 | fastq.gz | 3.0 GB | ||
EGAF50000277512 | fastq.gz | 3.2 GB | ||
EGAF50000277513 | fastq.gz | 3.3 GB | ||
EGAF50000277514 | fastq.gz | 3.5 GB | ||
EGAF50000277515 | fastq.gz | 3.6 GB | ||
EGAF50000277516 | fastq.gz | 3.4 GB | ||
EGAF50000277517 | fastq.gz | 2.3 GB | ||
EGAF50000277518 | fastq.gz | 3.1 GB | ||
EGAF50000277519 | fastq.gz | 3.3 GB | ||
EGAF50000277520 | fastq.gz | 848.9 MB | ||
EGAF50000277521 | fastq.gz | 2.4 GB | ||
EGAF50000277522 | fastq.gz | 5.3 GB | ||
EGAF50000277523 | fastq.gz | 793.7 MB | ||
EGAF50000277524 | fastq.gz | 276.0 MB | ||
EGAF50000277525 | fastq.gz | 297.9 MB | ||
EGAF50000277526 | fastq.gz | 846.2 MB | ||
EGAF50000277527 | fastq.gz | 1.8 GB | ||
EGAF50000277528 | fastq.gz | 3.6 GB | ||
EGAF50000277529 | fastq.gz | 3.7 GB | ||
EGAF50000277530 | fastq.gz | 302.0 MB | ||
EGAF50000277531 | fastq.gz | 856.8 MB | ||
EGAF50000277532 | fastq.gz | 1.9 GB | ||
EGAF50000277533 | fastq.gz | 281.2 MB | ||
EGAF50000277534 | fastq.gz | 1.2 GB | ||
EGAF50000277535 | fastq.gz | 2.3 GB | ||
EGAF50000277536 | fastq.gz | 2.3 GB | ||
EGAF50000277537 | fastq.gz | 534.6 MB | ||
EGAF50000277538 | fastq.gz | 1.1 GB | ||
EGAF50000277539 | fastq.gz | 2.1 GB | ||
EGAF50000277540 | fastq.gz | 507.0 MB | ||
EGAF50000277541 | fastq.gz | 2.1 GB | ||
EGAF50000277542 | fastq.gz | 2.1 GB | ||
EGAF50000277543 | fastq.gz | 506.0 MB | ||
EGAF50000277544 | fastq.gz | 1.1 GB | ||
EGAF50000277545 | fastq.gz | 2.1 GB | ||
60 Files (154.0 GB) |